These diseases have FDA approved genetically engineered cures that are available now. If you or a loved one has one of these diseases, you should get them cured ASAP.
From Peter Diamandis
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Here’s an unusual idea for using genetic engineering to prevent disease, where the target is not the human body but the bacteria in the microbiome:
https://www.science.org/doi/10.1126/science.adu8000
The gut microbiota has long been an aspirational target for clinical delivery of therapeutics. Successful therapy by this route depends on ensuring engraftment of the therapeutic organisms and their clearance after treatment. Whitaker et al . have engineered a strain of Bacteroides vulgatus , which is commonly found in the gut of healthy humans, with two genetic modules. One is therapeutic to rectify oxalate metabolism for preventing kidney stone formation, and the second adds multiple biosafety promoters that make the organism reliant on an essential nutrient, in this case porphyrin. Although the approach is very promising therapeutically, so far it is still encountering problems with horizontal gene transfer creating “biosafety escape” mutants.